Alpha-1 Antitrypsin Deficiency

Pulmonology

Overview

Definition

Genetic disorder leading to panacinar emphysema and liver disease.

Epidemiology

Varies globally depending on genetics, environment, or exposure.

Etiology & Risk Factors

  • AAT gene mutation (PiZZ phenotype).

Clinical Symptoms

  • Early-onset COPD (lower lobes)
  • jaundice/cirrhosis in childhood.

Clinical Approach

Diagnosis

  • Serum AAT levels
  • genetic testing.

Management

  • IV AAT augmentation therapy
  • avoid smoking.

Complications

  • Emphysema
  • Liver cirrhosis.